Entos and L-CMD Foundation partner to develop potentially curative gene therapy for L-CMD, a rare, fatal, childhood disease.

The organizations are betting they can develop a redosable genetic therapy for LMNA-related congenital muscular dystrophy that could be a cure.

RICHMOND, Texas -- Austin was 5 months old when his mom, Hannah Lowe, learned her son has a rare form of muscular dystrophy called L-CMD. "It's caused by a single letter change in his DNA," Hannah ...