Everyday Health on MSN

Diagnosed with late-onset Pompe disease (LOPD) — what should I do now?

Get expert advice on navigating your LOPD journey, from starting ERT treatments and building a specialist care team to ...
Everyday Health

Pompe Disease Treatment: Enzyme Replacement Therapy, Diet, Respiratory Care, and More

Enzyme replacement therapy (ERT), which provides a synthetic version of missing GAA enzyme, is the primary treatment for this condition. It’s not a cure, but it can address symptoms for people in all ...
WebMD

Managing Late-Onset Pompe Disease With Opfolda

Opfolda (miglustat) is a medicine taken with another medicine for certain people with late-onset Pompe disease. Pompe disease is a rare genetic disorder that is caused by an abnormal gene for a ...
Seeking Alpha

Dyne Therapeutics Presents New Preclinical Data Demonstrating the Potential of the FORCE™ Platform to Deliver Enzyme Replacement Therapy to Muscle and CNS in Pompe Disease

WALTHAM, Mass., June 24, 2024 (GLOBE NEWSWIRE) -- Dyne Therapeutics, Inc (DYN). (Nasdaq: DYN), a clinical-stage muscle disease company focused on advancing innovative life-transforming therapeutics ...